Discussions tagged “cysticfibrosis”

Orkambi has been a groundbreaking medication for those with cystic fibrosis (CF) who have the F508del mutation. It's designed to help the faulty protein in CF cells function better, which can significantly improve lung function and reduce other symptoms. However, like any medication, it comes with a range of side effects, some of which can be serious. I've been reading about the potential benefits and risks, and I'm curious to hear from others who have experience with Orkambi. What's been your journey with this medication? Have you noticed any significant improvements in your condition or have you encountered any troubling side effects?